4
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | 4-cyano-N-[2-(1-cyclohexen-1-yl)-4-[1-[dimethylamino)acetyl]-4-piperidinyl]phenyl]-1H-imidazole-2-carboxamide monohydrochlorideTipifarnib | Orphan Designation | - |
| heterotaxy, visceral, 1, X-linked | Doxil | Orphan Designation | - |
| mucopolysaccharidosis-plus syndrome | Doxil | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | Doxil | Orphan Designation | - |
| myelodysplastic syndrome | Epoetin alfa | Orphan Designation | - |
| plasma cell myeloma | Doxil | Orphan Designation | - |