3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| adult spinal cord glioblastoma | 5-(6,6-dimethyl-4-morpholino-8,9-dihydro-6H-[1,4]oxazino[3,4-e]purin-2-yl)pyrimidin-2-amine | Orphan Designation | - |
| atypical teratoid rhabdoid tumor | Paxalisib (INN and USAN) | Orphan Designation | - |
| brain glioblastoma | 5-(6,6-dimethyl-4-morpholino-8,9-dihydro-6H-[1,4]oxazino[3,4-e]purin-2-yl)pyrimidin-2-amine | Orphan Designation | - |
| glioblastoma | 5-(6,6-dimethyl-4-morpholino-8,9-dihydro-6H-[1,4]oxazino[3,4-e]purin-2-yl)pyrimidin-2-amine | Orphan Designation | - |
| malignant glioma | Paxalisib | Orphan Designation | - |
| rhabdoid tumor predisposition syndrome 1 | Paxalisib (INN and USAN) | Orphan Designation | - |
| rhabdoid tumor predisposition syndrome 2 | Paxalisib (INN and USAN) | Orphan Designation | - |