2
Orphan Designations
4
FDA Approvals
9
Rare Diseases
1
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| FGFR3-related chondrodysplasia | Crysvita | Orphan Designation | - |
| Oncogenic osteomalacia | Crysvita | Orphan Designation | - |
| X-linked dominant hypophosphatemic rickets | Crysvita | Orphan Designation | - |
| hypophosphatemic rickets, X-linked recessive | Crysvita | Orphan Designation | - |
| proteinuria, low molecular weight, with hypercalciuria and nephrocalcinosis | Crysvita | Orphan Designation | - |
| tumor grade X, general grading system | Crysvita | Orphan Designation | - |
| tumor of adipose tissue | Crysvita | Orphan Designation | - |
| tumor of cranial and spinal nerves | Crysvita | Orphan Designation | - |
| tumor of salivary gland | Crysvita | Orphan Designation | - |