6
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Niemann-Pick disease type C | allopregnanolone | Orphan Designation | - |
| Niemann-Pick disease, type C1 | allopregnanolone | Orphan Designation | - |
| Niemann-Pick disease, type C2 | allopregnanolone | Orphan Designation | - |
| fibrodysplasia ossificans progressiva | 3-(4-(8-fluoroquinoline)-Imidazole[1,2-a]pyridine-7-(1-phenyl-4-(1-(4-methyl piperazine)3-(4-(1,5-Napthrydine)-Imidazole[1,2-a]pyridine-7-(1-phenyl-4-(1-(4-methyl piperazine)4-(6-(4-(piperazin-1-yl)phenyl_pyrazolo[1,5-a]pyrimidin-3-yl)quinoline hydrochloride | Orphan Designation | - |
| lupus nephritis | Abetimus | Orphan Designation | - |
| malaria | artesunate | Orphan Designation | - |