9
Orphan Designations
0
FDA Approvals
15
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| atypical teratoid rhabdoid tumor | N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| diffuse large B-cell lymphoma | (+)N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| diffuse large B-cell lymphoma with chronic inflammation | (+)N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| hepatoblastoma | N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| hereditary spastic paraplegia 17 | (+)N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| large-cell immunoblastic lymphoma | (+)N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| malignant glioma | Hydroxyurea methylacylfulvene | Orphan Designation | - |
| malignant pancreatic neoplasm | N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| mantle cell lymphoma | (+)N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| primary pulmonary diffuse large B-cell lymphoma | (+)N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| rhabdoid tumor | N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| rhabdoid tumor predisposition syndrome 1 | N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| rhabdoid tumor predisposition syndrome 2 | N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| soft tissue sarcoma | (+)N-hydroxy-N(methylacylfulvene)ureaN-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |
| thyroid gland diffuse large B-cell lymphoma | (+)N-hydroxy-N-(methylacylfulvene)urea | Orphan Designation | - |