2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| abetalipoproteinemia | apolipoprotein E mimetic peptide (AEM-28(R)-14) | Orphan Designation | - |
| homozygous 11P15-p14 deletion syndrome | apolipoprotein E mimetic peptide (AEM-28(R)-14) | Orphan Designation | - |
| homozygous familial hypercholesterolemia | apolipoprotein E mimetic peptide (AEM-28(R)-14)apolipoprotein E mimetic peptide | Orphan Designation | - |