1
Orphan Designations
1
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| B-cell chronic lymphocytic leukemia | Elliotts B Solution | Orphan Designation | - |
| DYRK1A-related intellectual disability syndrome | Elliotts B Solution | Orphan Designation | - |
| anosmia for isobutyric acid | Elliotts B Solution | Orphan Designation | - |
| double nail for fifth toe | Elliotts B Solution | Orphan Designation | - |
| hemoglobin--variants for which the chain carrying the mutation 1S unknown or uncertain | Elliotts B Solution | Orphan Designation | - |
| meningeal melanocytoma | Elliotts B Solution | Orphan Designation | - |
| meningeal melanomatosis | Elliotts B Solution | Orphan Designation | - |
| meningeal sarcoma | Elliotts B Solution | Orphan Designation | - |
| meningeal tuberculosis | Elliotts B Solution | Orphan Designation | - |
| neuroacanthocytosis | Elliotts B Solution | Orphan Designation | - |