2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| carbon monoxide-induced delayed encephalopathy | Caveolin-1 Scaffolding Domain 7-Mer | Orphan Designation | - |
| coccidioidomycosis | single chain urokinase plasminogen activator | Orphan Designation | - |
| intestinal pseudoobstruction, neuronal, chronic idiopathic, X-linked | Caveolin-1 Scaffolding Domain 7-Mer | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | Caveolin-1 Scaffolding Domain 7-Mer | Orphan Designation | - |
| pleural empyema | single chain urokinase plasminogen activator | Orphan Designation | - |
| tuberculous empyema | single chain urokinase plasminogen activator | Orphan Designation | - |