1
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Toriello-Lacassie-Droste syndrome | small molecule inhibitor of the B-Raf protein | Orphan Designation | - |
| autoinflammation with arthritis and dyskeratosis | small molecule inhibitor of the B-Raf protein | Orphan Designation | - |
| autosomal recessive congenital ichthyosis 2 | small molecule inhibitor of the B-Raf protein | Orphan Designation | - |
| linear nevus sebaceous syndrome | small molecule inhibitor of the B-Raf protein | Orphan Designation | - |