2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| amyotrophic lateral sclerosis | repository corticortropin injection | Orphan Designation | - |
| selective peripheral resistance to thyroid hormone | Nitric Oxide | Orphan Designation | - |
| selective pituitary resistance to thyroid hormone | Nitric Oxide | Orphan Designation | - |