2
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Charcot-Marie-Tooth disease, axonal, mitochondrial form, 1 | Dynamine | Orphan Designation | - |
| Lambert-Eaton myasthenic syndrome | Dynamine | Orphan Designation | - |
| Roussy-Levy syndrome | Dynamine | Orphan Designation | - |
| distal hereditary motor neuropathy | Dynamine | Orphan Designation | - |
| hereditary motor neuron disease | Dynamine | Orphan Designation | - |