1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Wiskott-Aldrich syndrome | Apokyn | Orphan Designation | - |
| double nail for fifth toe | Apokyn | Orphan Designation | - |
| hairy palms and soles | Apokyn | Orphan Designation | - |
| infantile digital fibromatosis | Apokyn | Orphan Designation | - |
| motor neuron disorder | Apokyn | Orphan Designation | - |
| recessive aplasia cutis congenita of limbs | Apokyn | Orphan Designation | - |