3
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Fanconi renotubular syndrome 4 with maturity-onset diabetes of the young | Bispecific antibody 520c9x22 | Orphan Designation | - |
| Wolf-Hirschhorn syndrome | Monoclonal antibodies PM-81 and AML-2-23 | Orphan Designation | - |
| acute myeloid leukemia | Monoclonal antibody -81 | Orphan Designation | - |
| cerebrooculofacioskeletal syndrome 2 | Bispecific antibody 520c9x22 | Orphan Designation | - |
| double nail for fifth toe | Monoclonal antibodies PM-81 and AML-2-23 | Orphan Designation | - |
| hyperinsulinemic hypoglycemia, familial, 1 | Bispecific antibody 520c9x22 | Orphan Designation | - |
| intellectual disability, autosomal dominant 3 | Monoclonal antibodies PM-81 and AML-2-23 | Orphan Designation | - |
| spatial visualization, aptitude for | Monoclonal antibodies PM-81 and AML-2-23 | Orphan Designation | - |