2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| carbon monoxide-induced delayed encephalopathy | Implitapide | Orphan Designation | - |
| homozygous familial hypercholesterolemia | Implitapide | Orphan Designation | - |
| multisystemic smooth muscle dysfunction syndrome | Implitapide | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | Implitapide | Orphan Designation | - |