2
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Aicardi syndrome | Lioresal Intrathecal | Orphan Designation | - |
| band heterotopia of brain | Lioresal Intrathecal | Orphan Designation | - |
| chronic hiccup | Lioresal Intrathecal | Orphan Designation | - |
| intellectual disability-spasticity-ectrodactyly syndrome | Baclofen | Orphan Designation | - |
| microcephaly-brain defect-spasticity-hypernatremia syndrome | Baclofen | Orphan Designation | - |
| myoclonus, intractable, neonatal | Lioresal Intrathecal | Orphan Designation | - |
| neurodevelopmental disorder with cardiomyopathy, spasticity, and brain abnormalities | Lioresal Intrathecal | Orphan Designation | - |
| refractory celiac disease | Lioresal Intrathecal | Orphan Designation | - |
| spasticity-ataxia-gait anomalies syndrome | Baclofen | Orphan Designation | - |