1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Ewing sarcoma | modified messenger RNA encoding USP6 | Orphan Designation | - |
| Ewing sarcoma of bone | modified messenger RNA encoding USP6 | Orphan Designation | - |
| extraskeletal Ewing sarcoma | modified messenger RNA encoding USP6 | Orphan Designation | - |