2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| hyperphosphatasia with intellectual disability syndrome 6 | bovine lactoferrin | Orphan Designation | - |
| late-onset focal dermal elastosis | bovine lactoferrin | Orphan Designation | - |
| late-onset localized junctional epidermolysis bullosa-intellectual disability syndrome | bovine lactoferrin | Orphan Designation | - |
| late-onset retinal degeneration | bovine lactoferrin | Orphan Designation | - |
| necrotizing enterocolitis | bovine lactoferrin | Orphan Designation | - |
| perinatal necrotizing enterocolitis | bovine lactoferrin | Orphan Designation | - |