5
Orphan Designations
1
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Hodgkins lymphoma | N-(2-amino-phenyl)-4-[(4-pyridin-3-yl-pyrimidin-2-ylamino)-methyl] benzamide dihydrobromide | Orphan Designation | - |
| acute myeloid leukemia | N-(2-amino-phenyl)-4-[(4-pyridin-3-yl-pyrimidin-2-ylamino)-methyl] benzamide dihydrobromide | Orphan Designation | - |
| diffuse large B-cell lymphoma | mocetinostat | Orphan Designation | - |
| mesothelioma | (2M)-2-(4-(4-(aminomethyl)-1-oxo-1,2-dihydrophthalazin-6-yl)-1- methyl-1H-pyrazol-5-yl)-4-chloro-6-cyclopropoxy-3- fluorobenzonitrile | Orphan Designation | - |
| myelodysplastic syndrome | Mocetinostat | Orphan Designation | - |