1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Beemer-Langer syndrome | S-nitrosoglutathione | Orphan Designation | - |
| brain-lung-thyroid syndrome | S-nitrosoglutathione | Orphan Designation | - |
| cholestasis-pigmentary retinopathy-cleft palate syndrome | S-nitrosoglutathione | Orphan Designation | - |
| cranioectodermal dysplasia 2 | S-nitrosoglutathione | Orphan Designation | - |
| renal-hepatic-pancreatic dysplasia 1 | S-nitrosoglutathione | Orphan Designation | - |
| twin to twin transfusion syndrome | S-nitrosoglutathione | Orphan Designation | - |