Skip to main content
Diseases
Companies
News
Policy
About
Resources
Build with
KISHO
Sign In
Sign Up
Open menu
Kisho
National Institutes of Health, National Center for Advancing Translational Sciences — Rare Disease Pipeline | Kisho | Kisho
National Institutes of Health, National Center for Advancing Translational Sciences
Other
1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
propionic acidemia
Adeno-Associated Virus 9 human Propionyl-CoA Carboxylase, alpha subunit (AAV9-hPCCA)
Orphan Designation
-
← Back to Companies
