2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DYRK1A-related intellectual disability syndrome | Technetium Tc99m anti-melanoma murine monoclonal antibody | Orphan Designation | - |
| anosmia for isobutyric acid | Technetium Tc99m anti-melanoma murine monoclonal antibody | Orphan Designation | - |
| neuroacanthocytosis | Technetium Tc99m anti-melanoma murine monoclonal antibody | Orphan Designation | - |
| plasma cell myeloma | Chelating agent delivering Holmium-166 | Orphan Designation | - |