1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | polyethylene glycol-3350 | Orphan Designation | - |
| peripheral nerve lesion | polyethylene glycol-3350 | Orphan Designation | - |
| peripheral nerve schwannoma | polyethylene glycol-3350 | Orphan Designation | - |