4
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Angelman syndrome | cyclo(-L-Glycyl-L-2-Allylproline) | Orphan Designation | - |
| Phelan-McDermid syndrome | Cyclo(-L-Glycyl-L-2-Allylproline) | Orphan Designation | - |
| Pitt-Hopkins syndrome | Cyclo(-L-Glycyl-L-2-Allylproline) | Orphan Designation | - |
| Prader-Willi syndrome | Synthetic analogue of cyclic Glycine-Proline | Orphan Designation | - |