1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cerebrooculofacioskeletal syndrome 1 | sodium chlorite | Orphan Designation | - |
| microcephaly 13, primary, autosomal recessive | sodium chlorite | Orphan Designation | - |
| microcephaly-capillary malformation syndrome | sodium chlorite | Orphan Designation | - |