1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Carney-Stratakis syndrome | N( 4{[ 5fluoro7( 2methoxyethoxy) 4quinazolinyl] amino}phenyl)2( 4isopropyl1H1,2,3triazol1yl) acetamide 4-methylbenzenesulfonate (1:1) | Orphan Designation | - |
| colorectal gastrointestinal stromal tumor | N( 4{[ 5fluoro7( 2methoxyethoxy) 4quinazolinyl] amino}phenyl)2( 4isopropyl1H1,2,3triazol1yl) acetamide 4-methylbenzenesulfonate (1:1) | Orphan Designation | - |
| gastrointestinal stromal tumor | N( 4{[ 5fluoro7( 2methoxyethoxy) 4quinazolinyl] amino}phenyl)2( 4isopropyl1H1,2,3triazol1yl) acetamide 4-methylbenzenesulfonate (1:1) | Orphan Designation | - |