2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Phelan-McDermid syndrome | N-omega-propyl-l-arginine phosphate salt | Orphan Designation | - |
| malignant glioma | 7-Nitro-1H-indazole | Orphan Designation | - |