3
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| diabetes mellitus, transient neonatal, 1 | Group B streptococcus immune globulin | Orphan Designation | - |
| idiopathic neonatal atrial flutter | Group B streptococcus immune globulin | Orphan Designation | - |
| permanent neonatal diabetes mellitus 1 | Group B streptococcus immune globulin | Orphan Designation | - |
| pulmonary alveolar proteinosis with hypogammaglobulinemia | Mucoid exopolysaccharide Pseudomonas hyperimmune globulin | Orphan Designation | - |