1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| pediatric hepatocellular carcinoma | 9-nitro-20-(S)-camptothecin | Orphan Designation | - |
| pediatric ovarian dysgerminoma | 9-nitro-20-(S)-camptothecin | Orphan Designation | - |
| pediatric-onset Graves disease | 9-nitro-20-(S)-camptothecin | Orphan Designation | - |