2
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ALK+ histiocytosis | an orally bioavailable ALK inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| ALK-positive anaplastic large cell lymphoma | an orally bioavailable ROS1 inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| ALK-positive large B-cell lymphoma | an orally bioavailable ALK inhibitor (a macrocyclic compound containing nitrogen heterocycles)an orally bioavailable ROS1 inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| Ross river fever | an orally bioavailable ROS1 inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| X-linked retinoschisis | an orally bioavailable ROS1 inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| cardiac tamponade | an orally bioavailable ROS1 inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| continuous spikes and waves during sleep | an orally bioavailable ALK inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| lipoprotein types--Lt system | an orally bioavailable ALK inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| primary cutaneous diffuse large B-cell lymphoma, Leg type | an orally bioavailable ALK inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |
| sporotrichosis | an orally bioavailable ROS1 inhibitor (a macrocyclic compound containing nitrogen heterocycles) | Orphan Designation | - |