2
Orphan Designations
1
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Ross river fever | Ibtrozi | Orphan Designation | - |
| X-linked retinoschisis | Ibtrozi | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | Ibtrozi | Orphan Designation | - |
| cardiac tamponade | Ibtrozi | Orphan Designation | - |
| malignant glioma | CDK inhibitor (CDKI) of CDK2/4/6 | Orphan Designation | - |
| primary adult heart tumor | Ibtrozi | Orphan Designation | - |
| sporotrichosis | Ibtrozi | Orphan Designation | - |