3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| GM1 gangliosidosis | mecasermin rinfabate | Orphan Designation | - |
| arteriovenous malformations of the brain | mecasermin rinfabate (rhIGF-1/rhIGFBP-3) | Orphan Designation | - |
| bronchopulmonary dysplasia | mecasermin rinfabate | Orphan Designation | - |
| exudative vitreoretinopathy 1 | mecasermin rinfabate | Orphan Designation | - |
| retinopathy of prematurity | mecasermin rinfabate | Orphan Designation | - |