4
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute graft versus host disease | echinomycin | Orphan Designation | - |
| acute myeloid leukemia | echinomycin | Orphan Designation | - |
| adenoid cystic carcinoma | Gotistobart | Orphan Designation | - |
| cervical non-keratinizing squamous cell carcinoma | gotistobart | Orphan Designation | - |
| chronic graft versus host disease | echinomycin | Orphan Designation | - |
| graft versus host disease | echinomycin | Orphan Designation | - |
| non-small cell squamous lung carcinoma | gotistobart | Orphan Designation | - |
| vulvar non-keratinizing squamous cell carcinoma | gotistobart | Orphan Designation | - |