3
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| amyotrophic lateral sclerosis | levosimendan | Orphan Designation | - |
| desmoid tumor | Toremifene | Orphan Designation | - |
| familial adenomatous polyposis 1 | Toremifene | Orphan Designation | - |
| growth hormone insensitivity syndrome | Fareston | Orphan Designation | - |
| growth hormone-producing pituitary gland adenoma | Fareston | Orphan Designation | - |
| hormone receptor-positive breast cancer | Fareston | Orphan Designation | - |
| hormone-resistant breast carcinoma | Fareston | Orphan Designation | - |
| hormone-resistant prostate carcinoma | Fareston | Orphan Designation | - |
| metastatic malignant neoplasm in the colon | Fareston | Orphan Designation | - |
| tumor predisposition syndrome 3 | Toremifene | Orphan Designation | - |