3
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute graft versus host disease | thalidomide | Orphan Designation | - |
| chronic graft versus host disease | thalidomide | Orphan Designation | - |
| graft versus host disease | thalidomide | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 11 | Thalidomide | Orphan Designation | - |
| mitochondrial DNA maintenance syndrome | Thalidomide | Orphan Designation | - |
| respiratory failure | Aerosolized pooled immune globulin | Orphan Designation | - |
| respiratory syncytial virus bronchiolitis | Aerosolized pooled immune globulin | Orphan Designation | - |
| respiratory syncytial virus infectious disease | Aerosolized pooled immune globulin | Orphan Designation | - |