1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| autoinflammatory disease, multisystem, with immune dysregulation, X-linked | Perflubron | Orphan Designation | - |
| newborn respiratory distress syndrome | Perflubron | Orphan Designation | - |
| surfactant metabolism dysfunction, pulmonary, 1 | Perflubron | Orphan Designation | - |