1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| isolated congenital growth hormone deficiency | Ngenla | Orphan Designation | - |
| isolated growth hormone deficiency type IA | Ngenla | Orphan Designation | - |
| isolated growth hormone deficiency type IB | Ngenla | Orphan Designation | - |
| isolated growth hormone deficiency type II | Ngenla | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Ngenla | Orphan Designation | - |
| pediatric-onset Graves disease | Ngenla | Orphan Designation | - |