2
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bicervical bicornuate uterus with patent cervix and vagina | Rubraca | Orphan Designation | - |
| Char syndrome | Rubraca | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | Rubraca | Orphan Designation | - |
| hypophosphatasia | recombinant human alkaline phosphatase | Orphan Designation | - |
| multisystemic smooth muscle dysfunction syndrome | Rubraca | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | Rubraca | Orphan Designation | - |
| ovarian cancer | Rubraca | Orphan Designation | - |