1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| hereditary hypophosphatemic rickets with hypercalciuria | ATnativ | Orphan Designation | - |
| lymphedema-distichiasis syndrome | ATnativ | Orphan Designation | - |
| pancreatic hypoplasia-diabetes-congenital heart disease syndrome | ATnativ | Orphan Designation | - |