2
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Marshall-Smith syndrome | Dehydroepiandrosterone sulfate sodium | Orphan Designation | - |
| Wiedemann-Steiner syndrome | Dehydroepiandrosterone sulfate sodium | Orphan Designation | - |
| serous cystadenofibroma | Dehydroepiandrosterone sulfate sodium | Orphan Designation | - |
| serous otitis media | Dehydroepiandrosterone sulfate sodium | Orphan Designation | - |
| serous surface papilloma | Dehydroepiandrosterone sulfate sodium | Orphan Designation | - |