5
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Rett syndrome | Ketamine | Orphan Designation | - |
| amyotrophic lateral sclerosis | ketamine | Orphan Designation | - |
| brain ischemia | ketamine hydrochloride | Orphan Designation | - |
| complex regional pain syndrome | Ketamine | Orphan Designation | - |
| facioscapulohumeral muscular dystrophy | Ketamine | Orphan Designation | - |
| ischemia reperfusion injury | ketamine hydrochloride | Orphan Designation | - |
| malignant carotid body paraganglioma | Ketamine Hydrochloride | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | Ketamine | Orphan Designation | - |
| post-treatment Lyme disease syndrome | Ketamine Hydrochloride | Orphan Designation | - |
| retinal ischemia | ketamine hydrochloride | Orphan Designation | - |
| treatment-refractory schizophrenia | Ketamine Hydrochloride | Orphan Designation | - |