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Pharnext SA — Rare Disease Pipeline | Kisho | Kisho
Pharnext SA
Other
1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
Charcot-Marie-Tooth disease type 1A
(RS)-baclofen, naltrexone and D-sorbitol
Orphan Designation
-
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