2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| mantle cell lymphoma | allogeneic gene edited CD20-directed CAR (Chimeric Antigen Receptor) T cells | Orphan Designation | - |
| plasma cell myeloma | Allogeneic gene edited BCMA-directed CAR T cells | Orphan Designation | - |