5
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Hutchinson-Gilford progeria syndrome | progerinin | Orphan Designation | - |
| Werner syndrome | Progerinin | Orphan Designation | - |
| amyotrophic lateral sclerosis | amisodinAmisodin | Orphan Designation | - |
| neurofibromatosis | Trineumin | Orphan Designation | - |