1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| carbon monoxide-induced delayed encephalopathy | glycafilin | Orphan Designation | - |
| delayed membranous cranial ossification | glycafilin | Orphan Designation | - |
| delayed puberty, self-limited | glycafilin | Orphan Designation | - |