3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| choline deficiency disease | Choline chloride | Orphan Designation | - |
| congenital bile acid synthesis defect 4 | Choline chloride | Orphan Designation | - |
| congenital disorder of deglycosylation 1 | Choline chloride | Orphan Designation | - |
| lymphatic malformation | picibanil | Orphan Designation | - |
| lymphatic malformation 5 | picibanil | Orphan Designation | - |
| lymphatic malformation 6 | picibanil | Orphan Designation | - |
| multiple mitochondrial dysfunctions syndrome 3 | Choline chloride | Orphan Designation | - |