2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Duchenne muscular dystrophy | laminin-111 (human) | Orphan Designation | - |
| congenital merosin-deficient muscular dystrophy 1A | human laminin-111 | Orphan Designation | - |
| congenital myasthenic syndrome 10 | human laminin-111 | Orphan Designation | - |
| rigid spine muscular dystrophy 1 | human laminin-111 | Orphan Designation | - |