3
Orphan Designations
2
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Opitz G/BBB syndrome | Ethamolin | Orphan Designation | - |
| alveolar capillary dysplasia with misalignment of pulmonary veins | Ethamolin | Orphan Designation | - |
| anophthalmia/microphthalmia-esophageal atresia syndrome | Ethamolin | Orphan Designation | - |
| congenital sucrase-isomaltase deficiency | Sucraid | Orphan Designation | - |
| hypotonia-failure to thrive-microcephaly syndrome | ethanolamine | Orphan Designation | - |
| lip and oral cavity carcinoma | Sucraid | Orphan Designation | - |
| oral Crohn disease | Sucraid | Orphan Designation | - |
| oral cavity cancer | Sucraid | Orphan Designation | - |
| oral cavity neoplasm | Sucraid | Orphan Designation | - |
| oral mucosa leukoplakia | Sucraid | Orphan Designation | - |
| twin to twin transfusion syndrome | ethanolamine | Orphan Designation | - |