1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| MELAS syndrome | nicotinamide riboside | Orphan Designation | - |
| Stormorken syndrome | nicotinamide riboside | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 1 | nicotinamide riboside | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 13 | nicotinamide riboside | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 8a | nicotinamide riboside | Orphan Designation | - |
| mitochondrial neurogastrointestinal encephalomyopathy | nicotinamide riboside | Orphan Designation | - |