4
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 3-hydroxy-3-methylglutaric aciduria | Glyburide | Orphan Designation | - |
| Dubowitz syndrome | glyburide | Orphan Designation | - |
| PEHO syndrome | Glyburide | Orphan Designation | - |
| acute disseminated encephalomyelitis | Glyburideglyburide | Orphan Designation | - |
| acute flaccid myelitis | glyburide | Orphan Designation | - |
| acute lymphoblastic leukemia | glyburide | Orphan Designation | - |
| large cell carcinoma | glyburide | Orphan Designation | - |
| large congenital melanocytic nevus | glyburide | Orphan Designation | - |
| large-cell immunoblastic lymphoma | glyburide | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | glyburide | Orphan Designation | - |
| spinal muscular atrophy, distal, autosomal recessive, 6 | glyburide | Orphan Designation | - |