1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| autosomal recessive inherited pseudoxanthoma elasticum | zuretinol acetate | Orphan Designation | - |
| inherited retinal dystrophy | zuretinol acetate | Orphan Designation | - |
| maternally-inherited diabetes and deafness | zuretinol acetate | Orphan Designation | - |